Each rare disease may be uncommon, but having a rare disease isn’t. 1 in 17 people will have a rare disease at some point in their lives: that’s 3.5 million people in the UK alone. 75% of rare diseases affect children, and are often chronic or fatal: 30% of patients with rare diseases will die before their fifth birthday. There are 7,000 rare diseases, of which less than 5% have an approved treatment.
By repurposing existing drugs our approach can find potential treatments for these patients at a fraction of the time and cost of traditional drug discovery. We work directly with rare disease communities to understand patients’ needs and accelerate the translation of research into effective treatments.
At Healx you’ll have the chance to apply your skills and ideas to make a real difference to patients in need.